ODEVIXIBAT TREATMENT IN PATIENTS WITH FIC1 DEFICIENCY: SUSTAINED EFFICACY, PARTICULARLY IN PRURITUS, IN AN INTEGRATED ANALYSIS OF RESPONDERS (PEDFIC 1 AND PEDFIC 2)

Verkade, H;Thompson, R;Artan, R;Calvo, P L;Sokal, Etienne;et.al.
(2025) 57TH Annual Meeting of ESPGHAN — Location: Helsinski, Finland (14.May.2025)

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  • Verkade, H
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  • Thompson, Rorcid-logo
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  • Artan, R
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  • Calvo, P L
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  • Sokal, Etienneorcid-logoUCLouvain
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  • et. al.
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Abstract
ODEVIXIBAT TREATMENT IN PATIENTS WITH FIC1 DEFICIENCY: SUSTAINED EFFICACY, PARTICULARLY IN PRURITUS, IN AN INTEGRATED ANALYSIS OF RESPONDERS (PEDFIC 1 AND PEDFIC 2)
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Verkade, H., Thompson, R., Artan, R., Calvo, P. L., Czubkowski, P., Dalgic, B., d’Antonio, L., Durmaz, O., Grammatikopoulos, T., Gupte, G., Hardikar, W., Kamath, B., Lacaille F, Lainka, E., Loomes, K., Mack, C. L., McKiernan, P., Ozen, H., Rajwal, S., et al. (2025). ODEVIXIBAT TREATMENT IN PATIENTS WITH FIC1 DEFICIENCY: SUSTAINED EFFICACY, PARTICULARLY IN PRURITUS, IN AN INTEGRATED ANALYSIS OF RESPONDERS (PEDFIC 1 AND PEDFIC 2). 57TH Annual Meeting of ESPGHAN, Helsinski, Finland. https://hdl.handle.net/2078.5/244182