ODEVIXIBAT TREATMENT IN PATIENTS WITH FIC1 DEFICIENCY: SUSTAINED EFFICACY, PARTICULARLY IN PRURITUS, IN AN INTEGRATED ANALYSIS OF RESPONDERS (PEDFIC 1 AND PEDFIC 2)
Verkade, H;Thompson, R;Artan, R;Calvo, P L;Sokal, Etienne;et.al.
(2025) 57TH Annual Meeting of ESPGHAN — Location: Helsinski, Finland (14.May.2025)
ODEVIXIBAT TREATMENT IN PATIENTS WITH FIC1 DEFICIENCY: SUSTAINED EFFICACY, PARTICULARLY IN PRURITUS, IN AN INTEGRATED ANALYSIS OF RESPONDERS (PEDFIC 1 AND PEDFIC 2)
Verkade, H., Thompson, R., Artan, R., Calvo, P. L., Czubkowski, P., Dalgic, B., d’Antonio, L., Durmaz, O., Grammatikopoulos, T., Gupte, G., Hardikar, W., Kamath, B., Lacaille F, Lainka, E., Loomes, K., Mack, C. L., McKiernan, P., Ozen, H., Rajwal, S., et al. (2025). ODEVIXIBAT TREATMENT IN PATIENTS WITH FIC1 DEFICIENCY: SUSTAINED EFFICACY, PARTICULARLY IN PRURITUS, IN AN INTEGRATED ANALYSIS OF RESPONDERS (PEDFIC 1 AND PEDFIC 2). 57TH Annual Meeting of ESPGHAN, Helsinski, Finland. https://hdl.handle.net/2078.5/244182